Rare Diseases, Real Stories is a special podcast series that celebrates families who are transforming the world of rare diseases. In each episode, hear from parents about the challenges they face before and after their child is diagnosed, and the grief, strength, love and unwavering hope that guide them. Through their stories, you'll discover how their collaboration with UMass Chan Medical School researchers is driving innovation and fostering new rare disease treatments. Prepare to be moved, motivated and inspired by the real-life champions who are shaping the future of rare disease advocacy and research, one family at a time.
Rare Diseases, Real Stories is produced by the UMass Chan’s Office of Communications.
The Translational Institute for Molecular Therapeutics was formed to evaluate therapies for rare diseases for which few or no treatment options exist. The institute leverages UMass Chan Medical School’s extensive expertise in researching and developing gene therapies for early-stage clinical trials. Philanthropy plays a crucial role in these pioneering efforts by advancing groundbreaking research and bringing hope to families.
Sign up for weekly news emails
